Rare Disease Day 2023
Recent Posts
- Oh, the relief that comes when an educated expert arrives to help
- HAE gene-editing therapy NTLA-2002 receives RMAT designation
- Diagnosing and treating HAE most challenging across rural US
- CSL Behring to seek approval of garadacimab this year
- Canadian agency recommends cost of Orladeyo be covered
- On kites that fly with no wind, and other tales of not giving up
- Elder woman found to have acquired angiodemia after tongue swelling
- Phase 2 trial of NTLA-2002, HAE gene-editing therapy, to enroll in US
- Even adults need memory strategies for HAE therapies
- Orladeyo zeroes swelling attacks in HAE patients