• Preventative Haegarda Therapy Quickly Reduces Number of HAE Attacks, Trial Analysis Shows
  • Pharvaris Raises $66M to Advance Oral Therapy for Hereditary Angioedema
  • Study Supports Genetic Testing to Diagnose HAE of Unknown Cause
  • ‘Disorder’ Film Festival Offers Look at Siblings Touched by Rare Diseases
  • Firazyr Safely Treats Acute Attacks in Older Angiodema Patients, Study Reports
  • At NY Genome Center, Legal Expert Presents Ethical Dilemmas in Gene Editing
  • New Rat Model of HAE More Closely Mimics Human Disease
  • Nebraska’s Neena Nizar Seeks Cure for Jansen’s, One of World’s Rarest Diseases
  • Firazyr of Limited Help with Angioedema Caused by ACE Inhibitors, Pooled Trial Data Suggest
  • Oklahoma Ranks Lowest on Programs Key to Rare Diseases on NORD’s 2019 State Report Card
  • Rare Disease Groups Seek Public Support to Renew Newborn Screening Act in Senate
  • Regenxbio to Develop Antibody-based Gene Therapy for Hereditary Angioedema